Ladders to Cures Accelerator Meeting (L2CAM): Data-driven framework for optimized ASO selection in Duchenne Muscular Dystrophy by Michelle Rengarajan, MD, PhD

Date: Wed. 05/27/26

Time: 2:30 - 3:30PM ET

Location: Galapagos (75A-5-5001) and online at broad.io/L2CAM

Host: Jillian Shaw, PhD

Topic: Data-driven framework for optimized ASO selection in Duchenne Muscular Dystrophy

Speaker(s): Michelle Rengarajan, MD, PhD (Instructor in Medicine, Harvard Medical School; Physician, Massachusetts General Hospital; Associate Member, Broad Institute of MIT and Harvard)

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2025-2026 L2CAM Schedule:

10/15/25 Speaker(s): Masha Alimova, Oivin Guicherit, Ranjith Muraleedharan
Optical Screening Technologies and Approaches for Drug Discovery in Rare Diseases

11/12/25 Speaker(s): Brad Wertheim and George Alba
VEGF as a targetable node for pulmonary vascular diseases

12/10/25 Speaker(s): Alfred Pokmeng See
A proposal to develop scalable platforms to identify therapeutics for EPHB4-driven vein of galen malformation

2/4/26 Speaker(s): Matt Goddeeris
L2C: Every Cure

3/11/26 Speaker(s): Sami Farhi and Lindsey Erion Barner
L2C: STP Platform Capabilities

4/1/26 Speaker(s): Steve Carr and Namrata Udeshi
L2C: Proteomics

4/15/26 Speaker(s): Runxi Shen, Maria Lozada, Beth Cimini
Systematic rare disease phenotype and drug discovery - advances in imaging

5/27/26 Speaker(s): Michelle Rengarajan
Data-driven framework for optimized ASO selection in Duchenne Muscular Dystrophy

6/10/26 Speaker(s): Max Horlbeck Lab (Horlbeck Lab)
Therapeutic Strategies for Chromatinopathies