There are several ways to stay connected with the Ladders to Cures Accelerator. Please click here to join our L2C accelerator network. We will keep you in the loop on upcoming events and research highlights.

• Matchmaker Exchange

• JUMP Cell Painting Consortium

• Broad Drug Repurposing Hub

Please visit the Rare Genomes Project to learn more about patient-driven research studies aimed at discovering the genes underlying rare diseases.

• Global Genes: RARE Concierge

• n-Lorem Foundation

• Genetic and Rare Disease Information Center

• Genetic Alliance

• My Gene2

• Undiagnosed Diseases Network

• Rare Genomics Institute

• Rare Disease Clinical Research Network

While our work is intensely focused on understanding the rare genetic diseases that could benefit from our discoveries, we do not run any human clinical trials. As a research group, we work to identify the most promising, pre-clinical projects addressing nodal biology. We predominantly work with cell lines and animal models of human genetic diseases. Our vision is that the resulting research will enable scientists in industry or other clinical organizations to develop safe and effective therapeutics.

You can learn more about how clinical trials work here. To search for clinical trials that are relevant to you or your loved one, please visit: http://clinicaltrials.gov/. To access a curated list of gene and cell therapy trials, please visit the ASGCT Clinical Trials Finder. Please speak with your healthcare provider before enrolling in a clinical trial.